Tuesday, January 31, 2012

Amazing, Fantastic, Wonderful CF Drug Advancement Today!!!

Chances are you've already heard/read about the wonderful thing I'm going to post about if you're on CysticLife or you're my Facebook friend, but that's okay! It's too spectacular to not read it again!

This is how I feel right now!!
The FDA approved Kalydeco, the new drug that targets the underlying cause of CF in patients with the G551D mutation (ME!) - about 4% of the CF population!!!!! I'm currently 'too healthy', according to my CF doctor, to receive the drug right now, but that is a-okay with me. :-)

Here's what the Cystic Fibrosis Foundation had to say about it. 

Here's what the FDA had to say about it.

Here's what Vertex (the company who is producing the drug) had to say about it.

It's such an amazing feeling to know that all of the clinical trials/studies have definitely paid off! But it is SO important to keep spreading awareness and raising money so that the other 96% of CF patients can see their new medication come through the pipeline and get FDA approval, too. There are several clinical trials going on right now for a combination drug for those with CF with the most common mutation, Delta F508.

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